First ever RNA-based gene-silencing drug approved by FDA, and it's not cheap

Twenty years after the breakthrough discovery illustrating how RNA interference can be used to silence certain genes, and over a decade after the research won a Nobel prize, the U.S. Food and Drug Administration has approved the first drug utilizing this method for adult clinical treatment. The condition, hereditary transthyretin-mediated amyloidosis (hATTR), is rare and the drug is not a cure but rather an ongoing treatment that will reportedly cost up to US$450,000 per year for a single patient.

.. Continue Reading First ever RNA-based gene-silencing drug approved by FDA, and it's not cheap

Category: Medical

Tags:

• Drugs
• FDA
• RNA

from New Atlas https://ift.tt/2MGsJHk